ProQR intends to use the net proceeds from the offering, together with its existing cash and cash equivalents, to advance clinical development of its product candidates, to progress its other pipeline candidates, to advance its RNA-editing technology platforms, and for working capital and other general corporate purposes.

ProQR’s pipeline now includes two clinical programs, one preclinical program and two programs ready to enter development. “Since last year we have made good progress on executing on our strategy to develop life-changing therapies for patients in need, through a diversified pipeline with a balanced risk profile,” said Daniel A. de Boer, CEO of ProQR.

The company’s current pipeline includes potential treatments for rare genetic diseases including Leber's congenital amaurosis, (LCA10) dystrophic epidermolysis bullosa and Usher syndrome. ProQR intends to use the net proceeds from the offering, together with its existing cash and cash equivalents, to advance clinical development of its product candidates, to progress its other pipeline candidates, to advance its RNA-editing technology platforms, and for working capital and other general corporate purposes. 2021-03-24 · Shares of ProQR Therapeutics (NASDAQ:PRQR) were trading higher on Wednesday after the company released positive results from a clinical trial for one of its leading pipeline candidates, QR-421a. QR-313 is the short term catalyst amongst many that ProQR has in their pipeline. The company is expected to present Phase I/II interim data in the first quarter of 2019. With March newly here, the company is approaching the timeline that they set out.

Proqr pipeline

“We are pleased to see QR-421a advancing to pivotal testing and proud to support the work of ProQR as they advance their pipeline of RNA therapies to potentially help children, adults, and families who are affected by blindness caused by USH2A mutations and other rare inherited retinal diseases.” Phase 1/2 Stellar trial of QR-421a PRQR boasts a pipeline of 18 drug candidates, nearly all in early-stage development. Cash runway to last through to 2021 following recent public offering. ProQR is at the moment investigating two treatments for a rare genetic disease called Usher syndrome, QR-421a and QR-411. this pipeline can offer rewards for investors willing to wait for the ProQR Announces Positive Findings From an Interim Analysis in the Phase 1/2 trial of QR-421a for Usher Syndrome and Provides Business Update a deep pipeline of RNA therapies focused on “ProQR has expertise in antisense oligonucleotides, a productive platform, and a deep pipeline of novel RNA therapies focused on inherited retinal diseases, which fits well with our portfolio of ProQR was founded in 2012 by CEO Daniel de Boer and co-founders Henri Termeer, Dinko Valerio and Gerard Platenburg. The company’s current pipeline includes potential treatments for rare genetic diseases including Leber's congenital amaurosis, (LCA10) dystrophic epidermolysis bullosa and Usher syndrome. ProQR Therapeutics, a company focused on treating rare diseases, announced plans to advance its pipeline of RNA medicines to treat inherited retinal diseases to include two fully approved --ProQR Therapeutics N.V., a company dedicated to changing lives through the creation of transformative RNA therapies for inherited retinal diseases, today announced that it intends to offer and The product candidates in ProQR’s pipeline target diseases with a well-understood genetic cause where rational drug design can be applied to yield RNA molecules with therapeutic potential.

ProQR Therapeutics announced results from a planned analysis of its phase 1/2 Stellar trial of QR-421a in adults with Usher syndrome and non-syndromic retinitis pigmentosa (nsRP) due to USH2A exon 13 mutations.

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Illuminate Ph2 About ProQR ProQR Therapeutics is dedicated to changing lives through the creation of transformative RNA medicines for the treatment of severe orphan diseases such as cystic fibrosis and Leber’s congenital amaurosis. Based on our unique proprietary RNA repair platform technologies we are growing our pipeline with patients and loved ones in mind. Learn more about our Pipeline of RNA therapies.

2020-03-31

Page 1 of 6 work of ProQR as they advance their pipeline of RNA therapies to potentially. ProQR offers upbeat interim analysis in Phase 1/2 trial of QR-421a for Usher these data represent the second program from our ophthalmology pipeline that is Köp aktien ProQR Therapeutics N.V. - Ordinary Shares (PRQR).

Learn more about our Pipeline of RNA therapies. Patient-focused drug development When our CEO, Daniel A. de Boer, knew his newborn son had an incurable rare disease, he founded ProQR to help people like his son. Learn more. We aim to make a difference for these patients as we work to advance our pipeline of programs to treat inherited retinal diseases.” About QR-421a. QR- 421a is a Science & Pipeline SubmenuScience & Pipeline.
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We are on a mission “We are pleased to see QR-421a advancing to pivotal testing and proud to support the work of ProQR as they advance their pipeline of RNA therapies to potentially help children, adults, and families who are affected by blindness caused by USH2A mutations and other rare inherited retinal diseases.” Phase 1/2 Stellar trial of QR-421a Shares of ProQR Therapeutics (NASDAQ:PRQR) were trading higher on Wednesday after the company released positive results from a clinical trial for one of its leading pipeline candidates, QR-421a. LEIDEN, Netherlands and CAMBRIDGE, Mass., March 30, 2021 (GLOBE NEWSWIRE) -- ProQR Therapeutics N.V. (NASDAQ: PRQR), a company dedicated to changing lives through the creation of transformative RNA therapies for inherited retinal diseases (IRDs), today announced the pricing of its previously announced underwritten public offering of 13,846,154 ordinary shares at a price to the public of $6.50 per share. The therapies in the ProQR pipeline utilize an RNA oligonucleotide technology platform to repair genetic defects, targeting significant parts of the mutations that are known causes of inherited Wings Therapeutics has assumed control of ProQR’s pipeline dedicated to DEB and will take over the ongoing Phase 1/2 WINGS trial (NCT03605069) testing QR-313 for patients with recessive DEB due to mutations in exon 73 of the COL7A1 gene.

Learn more about our Pipeline of RNA therapies. Patient-focused drug development In order to achieve our goals, ProQR strives to integrate the patient voice into our decision-making throughout the drug development process as we believe that a patient-focused strategy is crucial to our success.
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31st March 2020: ProQR announce promising findings from an interim analysis in the Stellar Phase 1/2 clinical trial investigating QR-421a RNA therapy for Usher Syndrome. These results are based on data from the two patient cohorts, involving a total of 14 patients. The interim analysis results indicate the safety and efficacy of QR-421a to be appropriated in treating usher Syndrome and non

2021-03-25 2018-02-12 Agenda Overview and introduction by Daniel de Boer The relevance of the Nasal Potential Difference test in CF by JP Clancy, M.D. Results of the QR-010 NPD study by Noreen Henig, M.D. Pipeline and path ahead by Daniel de Boer Q&A session with JP Clancy, M.D., Noreen Henig, M.D., Smital Shah and Daniel de Boer ProQR Therapeutics 2 ProQR plans to independently advance its pipeline of RNA medicines to establish a multi-product, platform company in IRD. By 2023, the company expects its pipeline to have at least two commercial products, and at least three late-stage and seven early-stage programs in development. We are ProQR. About us; Vision 2023; Leadership; Careers; Contact; Science & Pipeline. Research and development pipeline; Clinical Trials.

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ProQR’s pipeline now includes two clinical programs, one preclinical program and two programs ready to enter development. “Since last year we have made good progress on executing on our strategy to develop life-changing therapies for patients in need, through a diversified pipeline with a balanced risk profile,” said Daniel A. de Boer, CEO of ProQR.

Research and development pipeline; Clinical Trials. QR-1123 Aurora phase 1/2 study for adRP; Sepofarsen ILLUMINATE phase 2/3 study for LCA10; QR-421a STELLAR phase 1/2 study for Usher syndrome; Sepofarsen INSIGHT – phase 1b/2 study for LCA10; Sepofarsen 2021-03-31 · ProQR Therapeutics N.V.: Investor Contact: Sarah Kiely ProQR Therapeutics N.V. T: +1 617 599 6228 skiely@proqr.com or Hans Vitzthum LifeSci Advisors T: +1 617 430 7578 hans@lifesciadvisors.com Overview (I bought in Friday at 13.80) ProQR is one of the many companies focusing their efforts on developing treatments and new medicines for rare … Summary. Ophthalmic RNA therapy concern ProQR Therapeutics N.V. (PRQR) has seen its share price more than half since its 2014 IPO. Promising Phase 1/2 data from its lead candidate (sepofarsen) has 2020-03-31 · ProQR Therapeutics N.V. Investor Contact: Sarah Kiely ProQR Therapeutics N.V. T: +1 617 599 6228 skiely@proqr.com or Hans Vitzthum LifeSci Advisors T: +1 617 430 7578 hans@lifesciadvisors.com 2020-07-14 · ProQR Therapeutics N.V. Investor Contact: Sarah Kiely ProQR Therapeutics N.V. T: +1 617 599 6228 skiely@proqr.com or Hans Vitzthum LifeSci Advisors T: +1 617 535 7743 hans@lifesciadvisors.com To navigate items, use the arrow, home, and end keys. Our Company. About PTC Therapeutics menu item, submenu.